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Lentiviral and genome-editing strategies for the treatment of β-hemoglobinopathies.
Marina Cavazzana, Annarita Miccio
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Blood2019 Dec 13Pmid / DOI:
31467062 -
Gene therapy of hemoglobinopathies: progress and future challenges.
Marina Cavazzana
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Hum. Mol. Genet.2019 Dec 13Pmid / DOI:
31322165 -
Anatomical and functional abnormalities on MRI in kabuki syndrome.
Nathalie Boddaert, Stanislas Lyonnet, Marlène Rio, Monica Zilbovicius , Jennifer Boisgontier, Jean-Marc Tacchella, Hervé Lemaître, Ana Saitovitch, Elza Rechtman, Ludovic Fillon
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Neuroimage Clin2019 Dec 11Pmid / DOI:
30497982 -
Overall Survival with Ribociclib plus Fulvestrant in Advanced Breast Cancer.
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N. Engl. J. Med.2019 Dec 11Pmid / DOI:
31826360 -
Annarita Miccio
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Mol. Ther.2019 Dec 11Pmid / DOI:
30424953 -
Heterogeneous clinical phenotypes and cerebral malformations reflected by rotatin cellular dynamics.
Nadia Bahi-Buisson
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Brain2019 Dec 10Pmid / DOI:
30879067 -
Fetal fraction and noninvasive prenatal testing: What clinicians need to know.
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Prenat. Diagn.2019 Dec 10Pmid / DOI:
31821597 -
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J. Clin. Lab. Anal.2019 Dec 10Pmid / DOI:
31821609 -
Intracellular offspring released from SFB filaments are flagellated.
Nadine CERF-BENSUSSAN
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Nat Microbiol2019 Dec 10Pmid / DOI:
31819216 -
Jean-Laurent CASANOVA , Emmanuelle Jouanguy, Laurent Abel
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J. Exp. Med.2019 Dec 9Pmid / DOI:
31270247 -
Jean-Laurent CASANOVA
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J. Clin. Invest.2019 Dec 9Pmid / DOI:
30422821 -
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J. Biol. Chem.2019 Dec 7Pmid / DOI:
31811089 -
Geneviève de Saint Basile, Alain Fischer, Fernando Sepulveda , Frédéric Guérin
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Front Immunol2019 Dec 7Pmid / DOI:
31787977 -
Chronic inflammation in the etiology of disease across the life span.
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Nat. Med.2019 Dec 6Pmid / DOI:
31806905 -
Jean-Laurent CASANOVA , Laurent Abel
Source :
Nat. Med.2019 Dec 6Pmid / DOI:
31806906